Roche halts development of drug candidate for muscle diseases, Chugai says

The company discontinued developing emugrobart after two studies showed the drug didn’t achieve intended outcomes.

Sarepta Therapeutics shares rise on early promise for rare disease drugs

Shares of Cambridge-based Sarepta rose about 35 percent in trading Wednesday after the company presented preliminary data on ...
Henley Standard

Father ‘broken’ by delay to access drug to fight son’s muscle wasting disease

THE father of a boy with a severe muscle wasting condition said waiting more than a year for regulatory approval of a drug to ...
Clinical Trials Arena on MSN

Roche drops phase III plans for emugrobart in two muscle wasting diseases

The big pharma company will no longer progress emugrobart to late-stage trials in FSHD and SMA due to a lack of efficacy.
Fierce Biotech

Genentech antibody fails to boost muscle in rare diseases, raising questions for obesity trial

Genentech is halting development of an antibody for two rare genetic diseases after the candidate failed to boost muscle ...

Treating disease at birth: How a brief spike in testosterone sets the trajectory for disease that appears decades later

Spinal and bulbar muscular atrophy (SBMA) is a rare inherited disease that causes progressive muscle weakness and wasting in ...
lex18

Family chooses hope over fear in battle against rare genetic muscle disease

RUSSELL COUNTY, Ky. (LEX 18) — A mother's love drives her to pursue experimental treatment as two of her four children battle a rare genetic disease that slowly weakens their muscles. Laura Moore says ...
EurekAlert!

Muscle wasting reversed in patients with rheumatoid arthritis

Patients with rheumatoid arthritis increased their leg muscle volume when treated with an anti-rheumatic drug, offering new hope for improved muscle health. Publishing in the prestigious journal, The ...